Duchenne Muscular Dystrophy Pipeline Drugs Assessment: Clinical Trails Analysis, Player Profiles, Collaborations, Key Targets, Geographic Focus, and Data Publications, 2019 - 2030

Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Clinical Trails Analysis, Player Profiles, Collaborations, Key Targets, Geographic Focus, and Data Publications, 2019 - 2030

Duchenne muscular dystrophy is a genetic disorder which causes progressive muscle degeneration and weakness, and it is one of the nine types of muscular dystrophy. Duchenne muscular dystrophy mostly affects males, but in rare cases occurs in females. Onset of the disease is generally 3 to 4 years of age and begins on hips, pelvic region, shoulders, and upper legs. Symptoms may include delayed or difficulty inability to stand, walk and difficulty in speaking.

Disease is diagnosed through the patient history, blood test for creatinine phosphokinase levels, molecular genetic testing, and muscle biopsy. There is no cure available for the disease till now. But the medications are available forrelieving the symptoms of the disease. Eteplirsen is used to treat the patients with specific gene mutation of gene that leads to DMD. Deflazacort, approved in 2017, becoming first corticosteroid to treat Duchenne muscular dystrophy.

 Key Developments:

  • In November 2016, Wave Life Sciences Ltd. Initiated the Phase I clinical trial for WVE-210201 Duchenne muscular dystrophy patients amenable to exon 51 skipping.

 

 

 

Duchenne Muscular Dystrophy Pipeline Drugs Assessment Dynamics

Duchenne Muscular Dystrophy Pipeline Drugs Assessment report studies the various therapeutics under clinical development for XYX treatment along with targets for various drug candidate. The report provides plethora of information pertaining to trail phases, companies involved in the Duchenne muscular dystrophy pipeline drugsdevelopment. This report studies the dynamics of the Duchenne Muscular Dystrophy Pipeline Drugs i.e. drivers, challenges,andopportunities which are significantly impacting the product development. The report provides various information pertaining the clinical trials such as designation, grants, patents, and technology among others. Moreover, the report on Duchenne muscular dystrophy pipeline drugs assessment comprehensively presents the geographic location, trial status information along with key players involved in the therapeutics development.

 

Duchenne Muscular Dystrophydmd Pipeline Drugs Assessment Segmentation Analysis

Report Benchmarks

Details

By formulation

  • Oral
  • Parenteral
  • Others

By therapy

  • Exon Skipping
  • Gene Therapy
  • Corticosteroids
  • Others

By trial phase

  • Phase I
  • Phase II
  • Phase III
  • Phase IV

 

By company

  • Pfizer Inc. (U.S.)
  • ReveraGenBioPharma, Inc. (U.S.)
  • Sarepta Therapeutics Inc. (U.S.)
  • Daiichi Sankyo Company (Japan)
  • BioMarin Pharmaceutical Inc. (U.S.)
  • NS Pharma, Inc. (Japan)
  • TAIHO PHARMACEUTICAL CO. (Japan)

 

Key Features of the Report

  • The report provides granular level information about the market size, regional market share, historic market (2019-2023), and forecast (2024-2030)
  • The report covers in-detail insights about the competitor’s overview, company share analysis, key market developments, and key strategies
  • The report outlines drivers, restraints, unmet needs, and trends that are currently affecting the market
  • The report tracks recent innovations, key developments, and start-up details that are actively working in the market
  • The report provides a plethora of information about market entry strategies, regulatory framework, and reimbursement scenario
  • The report analyses the impact of the socio-political environment through PESTLE Analysis and competition through Porter's Five Force Analysis

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Frequently Asked Questions

2021 is the base year and 2028 is the forecast year.

The report covers the five regions and 15+ countries market data: North America (United States, Canada), Europe (Germany, France, Italy, Spain, and United Kingdom (UK), Asia Pacific (China, India, Japan, Australia & New Zealand), Latin America (Brazil, Mexico, Argentina) and Middle East and Africa (Saudi Arabia, United Arab Emirates, South Africa).

In our report, we provide 12-15 market players’ information into the report. However, based on the client’s request we will provide additional country and regional market players information as well.

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Author

Muni Kumar Meravath

Muni Kumar Meravath is a seasoned Healthcare Market Research Analyst with over 6 years of experience in the healthc.....

  1. Executive Summary
  2. Global Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market Introduction
    • Global Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market Taxonomy
    • Global Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market Definitions
      • Formulation
      • Therapy
      • Trial Phase
  1. Global Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market Dynamics
    • Drivers
    • Restraints
    • Opportunities/Unmet Needs of the Market
    • Trends
    • Global Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market Dynamic Factors - Impact Analysis
    • Global Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market Competition Landscape
    • Epidemiology
  2. Global Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030
    • Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
    • Year-over-Year (Y-o-Y) Growth Analysis (%)
    • Market OpportunityAnalysis
  3. Global Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market, By Formulation, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
    • Oral
      • Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Parenteral
      • Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Others
      • Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
  1. Global Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market Forecast, By Therapy,2019 - 2023 and Forecast, 2024 - 2030
    • Exon Skipping
      • Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Gene Therapy
      • Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Corticosteroids
      • Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Others
      • Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
  1. Global Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market Forecast, By Trial Phase,2019 - 2023 and Forecast, 2024 - 2030
    • Phase I
      • Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Phase II
      • Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Phase III
      • Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Phase IV
      • Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
  1. Global Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market Forecast, By Region, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
    • North America
      • Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Europe
      • Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Asia-Pacific
      • Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Latin America
      • Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Middle East and Africa
      • Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Global Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market - Opportunity Analysis Index, By Formulation, By Therapy, By Trial Phase, and Region, 2024 - 2030
  2. North America Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment MarketAnalysis,2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
    • Formulation Analysis 2019 - 2023 and Forecast 2024 - 2030 by Revenue (USD Mn), Y-o-Y Growth (%), and Market Share (%)
      • Oral
      • Parenteral
      • Others
    • Therapy Analysis 2019 - 2023 and Forecast 2024 - 2030 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Exon Skipping
      • Gene Therapy
      • Corticosteroids
      • Others
    • Trial Phase Analysis 2019 - 2023 and Forecast 2024 - 2030 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Phase I
      • Phase II
      • Phase III
      • Phase IV
    • Country Analysis 2016 and Forecast 2024 - 2030 by Revenue (USD Mn) Y-o-Y Growth (%) and Market Share (%)
      • S.
      • Canada
    • North America Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market - Opportunity Analysis Index, By Formulation, By Therapy, By Trial Phase, and Country, 2024 - 2030
    • North America Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market Dynamics Trends
  3. Europe Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
    • Formulation Analysis 2019 - 2023 and Forecast 2024 - 2030 by Revenue (USD Mn), Y-o-Y Growth (%), and Market Share (%)
      • Oral
      • Parenteral
      • Others
    • Therapy Analysis 2019 - 2023 and Forecast 2024 - 2030 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Exon Skipping
      • Gene Therapy
      • Corticosteroids
      • Others
    • Trial Phase Analysis 2019 - 2023 and Forecast 2024 - 2030 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Phase I
      • Phase II
      • Phase III
      • Phase IV
    • Country Analysis 2019 - 2023 and Forecast 2024 - 2030 by Revenue (USD Mn) Y-o-Y Growth (%) and Market Share (%)
      • Germany
      • UK
      • France
      • Spain
      • Italy
      • Russia
      • Poland
      • Rest of Europe
    • Europe Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market - Opportunity Analysis Index, By Formulation, By Therapy, By Trial Phase, and Country, 2024 - 2030
    • Europe Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market Dynamics Trends
  4. Asia-Pacific Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
    • Formulation Analysis 2019 - 2023 and Forecast 2024 - 2030 by Revenue (USD Mn), Y-o-Y Growth (%), and Market Share (%)
      • Oral
      • Parenteral
      • Others
    • Therapy Analysis 2019 - 2023 and Forecast 2024 - 2030 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Exon Skipping
      • Gene Therapy
      • Corticosteroids
      • Others
    • Trial Phase Analysis 2019 - 2023 and Forecast 2024 - 2030 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Phase I
      • Phase II
      • Phase III
      • Phase IV
    • Country Analysis2019 - 2023 and Forecast 2024 - 2030 by Revenue (USD Mn) Y-o-Y Growth (%) and Market Share (%)
      • Japan
      • China
      • India
      • ASEAN
      • Australia & New Zealand
      • Rest of Asia-Pacific
    • Asia-Pacific Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market - Opportunity Analysis Index, By Formulation, By Therapy, By Trial Phase, and Country, 2024 - 2030
    • Asia-Pacific Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market Dynamics Trends
  5. Latin America Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
    • Formulation Analysis 2019 - 2023 and Forecast 2024 - 2030 by Revenue (USD Mn), Y-o-Y Growth (%), and Market Share (%)
      • Oral
      • Parenteral
      • Others
    • Therapy Analysis 2019 - 2023 and Forecast 2024 - 2030 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Exon Skipping
      • Gene Therapy
      • Corticosteroids
      • Others
    • Trial Phase Analysis 2019 - 2023 and Forecast 2024 - 2030 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Phase I
      • Phase II
      • Phase III
      • Phase IV
    • Country Analysis 2019 - 2023 and Forecast 2024 - 2030 by Revenue (USD Mn) Y-o-Y Growth (%) and Market Share (%)
      • Brazil
      • Mexico
      • Argentina
      • Venezuela
      • Rest of Latin America
    • Latin America Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market - Opportunity Analysis Index, By Formulation, By Therapy, By Trial Phase, and Country, 2024 - 2030
    • Latin America Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market Dynamics Trends
  6. Middle East and Africa Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030 (Revenue, USD Mn)
    • Formulation Analysis 2019 - 2023 and Forecast 2024 - 2030 by Revenue (USD Mn),Y-o-Y Growth (%), and Market Share (%)
      • Oral
      • Parenteral
      • Others
    • Therapy Analysis 2019 - 2023 and Forecast 2024 - 2030 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Exon Skipping
      • Gene Therapy
      • Corticosteroids
      • Others
    • Trial Phase Analysis 2019 - 2023 and Forecast 2024 - 2030 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Phase I
      • Phase II
      • Phase III
      • Phase IV
    • Country Analysis 2019 - 2023 and Forecast 2024 - 2030 by Revenue (USD Mn) Y-o-Y Growth (%) and Market Share (%)
      • Gulf Cooperation Council (GCC) Countries
      • Israel
      • South Africa
      • Rest of MEA
    • MEA Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market - Opportunity Analysis Index, By Formulation, By Therapy, By Trial Phase, and Country, 2024 - 2030
    • MEA Duchenne Muscular Dystrophy (DMD) Pipeline Drugs Assessment Market Dynamics Trends
  7. Competition Landscape
    • Strategic Dashboard of Top Market Players
    • Company Profiles (Introduction, Financial Analysis, Formulation& Service Offerings, Key Developments, Strategies, and SWOT Analysis)
      • Pfizer Inc. (U.S.)
      • ReveraGenBioPharma, Inc. (U.S.)
      • Sarepta Therapeutics Inc. (U.S.)
      • Daiichi Sankyo Company (Japan)
      • BioMarin Pharmaceutical Inc. (U.S.)
      • NS Pharma, Inc. (Japan)
      • TAIHO PHARMACEUTICAL CO. (Japan)
  1. Research Methodology
  2. Key Assumptions and Acronyms

 

Key Market Players

  • Pfizer Inc. (U.S.)
  • ReveraGenBioPharma, Inc. (U.S.)
  • Sarepta Therapeutics Inc. (U.S.)
  • Daiichi Sankyo Company (Japan)
  • BioMarin Pharmaceutical Inc. (U.S.)
  • NS Pharma, Inc. (Japan)
  • TAIHO PHARMACEUTICAL CO. (Japan)

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