Author
Muni Kumar Meravath is a seasoned Healthcare Market Research Analyst with over 6 years of experience in the healthc.....
Rare Hematology Disorders Market: By Disease Indication, By Treatment, By Patient, and By Geography
Rare Hematology Disorders market size was valued at US$ 14.3 billion in 2023 and is poised to grow at a CAGR of 5.7% from 2024 to 2030. The market is poised for significant growth in the coming years, driven by increased awareness of rare blood disorders, coupled with advancements in diagnostic techniques like genetic testing, several governments have implemented policies and incentives to encourage research and development of treatments for rare diseases, including rare blood disorders. These initiatives provide financial and regulatory support, This, in turn, fuels the market for treatment options. Despite the promising growth potential, the rare hematology disorders market also faces some challenges like the high cost of treatment, fragmented market, and limited clinical trial data, due to the small patient population, conducting extensive clinical trials for rare blood disorders can be challenging.
Further, several key trends are shaping the future of the rare hematology disorders market focusing on personalized medicine, a rise of gene therapies which creates an opportunity for developing Orphan drug designation and exclusivity in emerging markets by collaboration between pharmaceutical companies, academic institutions, and patient advocacy groups can accelerate research and development efforts, leading to the creation of more effective and affordable treatments for rare blood disorders.
Study Period
2024 - 2030Base Year
2023CAGR
5.7%Largest Market
Asia PacificFastest Growing Market
Asia Pacific
The market is experiencing significant growth driven by rising awareness and diagnosis, growing demand for specialized treatments, government support and orphan drug incentives, and technological advancements in gene editing, and gene therapy, which are leading to earlier and more accurate diagnoses, the demand for specialized and targeted therapies is rising. This creates opportunities for pharmaceutical companies to develop novel drugs and treatment modalities and other biotechnologies that offer promising avenues for developing curative treatments for rare blood disorders, and the market is witnessing a growing shift towards personalized medicine, tailoring treatments to individual patient's specific genetic makeup and disease characteristics. This approach holds promise for improving treatment efficacy and patient outcomes. These innovations hold immense potential to revolutionize the market landscape.
Report Benchmarks |
Details |
Report Study Period |
2024 - 2030 |
Market Size in 2023 |
US$ 14.3 billion |
Market CAGR |
5.7% |
By Disease Indication |
|
By Treatment |
|
By Patient |
|
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Rare hematology disorders Market market size was valued at US$ 14.3 billion in 2023 and is expected to grow at a CAGR of 5.7% from 2024 to 2030.
Novo Nordisk A/S, Sanofi, PRA Health Sciences, Celgene Corporation, Alexion Pharmaceuticals, Inc.. Bayer Healthcare AG, CSL Behring, Shire PLC, Pfizer Inc., Celgene Corporation, Amgen Inc., Novartis AG, Bristol Myers Squibb, F. Hoffmann-La Roche Ltd, Emmaus Medical, Inc.
Asia-Pacific is the fastest growing and North America is the dominant market in rare hematology disorders market.
1.Executive Summary |
2.Global Rare Hematology Disorders Market Introduction |
2.1.Global Rare Hematology Disorders Market - Taxonomy |
2.2.Global Rare Hematology Disorders Market - Definitions |
2.2.1.Disease Indication |
2.2.2.Treatment |
2.2.3.Patient |
2.2.4.Region |
3.Global Rare Hematology Disorders Market Dynamics |
3.1. Drivers |
3.2. Restraints |
3.3. Opportunities/Unmet Needs of the Market |
3.4. Trends |
3.5. Product Landscape |
3.6. New Product Launches |
3.7. Impact of COVID 19 on Market |
4.Global Rare Hematology Disorders Market Analysis, 2019 - 2023 and Forecast 2024 - 2030 |
4.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million) |
4.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) |
4.3. Market Opportunity Analysis |
5.Global Rare Hematology Disorders Market By Disease Indication, 2019 - 2023 and Forecast 2024 - 2030 (Sales Value USD Million) |
5.1. Rare blood cancers, |
5.1.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million) |
5.1.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) |
5.1.3. Market Opportunity Analysis |
5.2. Platelet-based disorders |
5.2.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million) |
5.2.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) |
5.2.3. Market Opportunity Analysis |
5.3. Plasma-based disorders |
5.3.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million) |
5.3.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) |
5.3.3. Market Opportunity Analysis |
5.4. Others |
5.4.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million) |
5.4.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) |
5.4.3. Market Opportunity Analysis |
6.Global Rare Hematology Disorders Market By Treatment, 2019 - 2023 and Forecast 2024 - 2030 (Sales Value USD Million) |
6.1. Recombinant factors |
6.1.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million) |
6.1.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) |
6.1.3. Market Opportunity Analysis |
6.2. Plasma-derived factors |
6.2.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million) |
6.2.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) |
6.2.3. Market Opportunity Analysis |
6.3. Gene therapies |
6.3.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million) |
6.3.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) |
6.3.3. Market Opportunity Analysis |
6.4. Other therapies |
6.4.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million) |
6.4.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) |
6.4.3. Market Opportunity Analysis |
7.Global Rare Hematology Disorders Market By Patient, 2019 - 2023 and Forecast 2024 - 2030 (Sales Value USD Million) |
7.1. Adults |
7.1.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million) |
7.1.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) |
7.1.3. Market Opportunity Analysis |
7.2. Paediatrics |
7.2.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million) |
7.2.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) |
7.2.3. Market Opportunity Analysis |
8.Global Rare Hematology Disorders Market By Region, 2019 - 2023 and Forecast 2024 - 2030 (Sales Value USD Million) |
8.1. North America |
8.1.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million) |
8.1.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) |
8.1.3. Market Opportunity Analysis |
8.2. Europe |
8.2.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million) |
8.2.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) |
8.2.3. Market Opportunity Analysis |
8.3. Asia Pacific (APAC) |
8.3.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million) |
8.3.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) |
8.3.3. Market Opportunity Analysis |
8.4. Middle East and Africa (MEA) |
8.4.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million) |
8.4.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) |
8.4.3. Market Opportunity Analysis |
8.5. Latin America |
8.5.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million) |
8.5.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) |
8.5.3. Market Opportunity Analysis |
9.North America Rare Hematology Disorders Market ,2019 - 2023 and Forecast 2024 - 2030 (Sales Value USD Million) |
9.1. Disease Indication Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
9.1.1.Rare blood cancers, |
9.1.2.Platelet-based disorders |
9.1.3.Plasma-based disorders |
9.1.4.Others |
9.2. Treatment Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
9.2.1.Recombinant factors |
9.2.2.Plasma-derived factors |
9.2.3.Gene therapies |
9.2.4.Other therapies |
9.3. Patient Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
9.3.1.Adults |
9.3.2.Paediatrics |
9.4. Country Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
9.4.1.United States of America (USA) |
9.4.2.Canada |
10.Europe Rare Hematology Disorders Market ,2019 - 2023 and Forecast 2024 - 2030 (Sales Value USD Million) |
10.1. Disease Indication Analysis and Forecast by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
10.1.1.Rare blood cancers, |
10.1.2.Platelet-based disorders |
10.1.3.Plasma-based disorders |
10.1.4.Others |
10.2. Treatment Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
10.2.1.Recombinant factors |
10.2.2.Plasma-derived factors |
10.2.3.Gene therapies |
10.2.4.Other therapies |
10.3. Patient Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
10.3.1.Adults |
10.3.2.Paediatrics |
10.4. Country Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
10.4.1.Germany |
10.4.2.France |
10.4.3.Italy |
10.4.4.United Kingdom (UK) |
10.4.5.Spain |
11.Asia Pacific (APAC) Rare Hematology Disorders Market ,2019 - 2023 and Forecast 2024 - 2030 (Sales Value USD Million) |
11.1. Disease Indication Analysis and Forecast by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
11.1.1.Rare blood cancers, |
11.1.2.Platelet-based disorders |
11.1.3.Plasma-based disorders |
11.1.4.Others |
11.2. Treatment Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
11.2.1.Recombinant factors |
11.2.2.Plasma-derived factors |
11.2.3.Gene therapies |
11.2.4.Other therapies |
11.3. Patient Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
11.3.1.Adults |
11.3.2.Paediatrics |
11.4. Country Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
11.4.1.China |
11.4.2.India |
11.4.3.Australia and New Zealand (ANZ) |
11.4.4.Japan |
11.4.5.Rest of APAC |
12.Middle East and Africa (MEA) Rare Hematology Disorders Market ,2019 - 2023 and Forecast 2024 - 2030 (Sales Value USD Million) |
12.1. Disease Indication Analysis and Forecast by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
12.1.1.Rare blood cancers, |
12.1.2.Platelet-based disorders |
12.1.3.Plasma-based disorders |
12.1.4.Others |
12.2. Treatment Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
12.2.1.Recombinant factors |
12.2.2.Plasma-derived factors |
12.2.3.Gene therapies |
12.2.4.Other therapies |
12.3. Patient Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
12.3.1.Adults |
12.3.2.Paediatrics |
12.4. Country Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
12.4.1.GCC Countries |
12.4.2.South Africa |
12.4.3.Rest of MEA |
13.Latin America Rare Hematology Disorders Market ,2019 - 2023 and Forecast 2024 - 2030 (Sales Value USD Million) |
13.1. Disease Indication Analysis and Forecast by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
13.1.1.Rare blood cancers, |
13.1.2.Platelet-based disorders |
13.1.3.Plasma-based disorders |
13.1.4.Others |
13.2. Treatment Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
13.2.1.Recombinant factors |
13.2.2.Plasma-derived factors |
13.2.3.Gene therapies |
13.2.4.Other therapies |
13.3. Patient Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
13.3.1.Adults |
13.3.2.Paediatrics |
13.4. Country Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) |
13.4.1.Brazil |
13.4.2.Mexico |
13.4.3.Rest of LA |
14. Competition Landscape |
14.1. Market Player Profiles (Introduction, Brand/Product Sales, Financial Analysis, Product Offerings, Key Developments, Collaborations, M & A, Strategies, and SWOT Analysis) |
14.2.1.Sanofi |
14.2.2.Novo Nordisk A/S |
14.2.3.PRA Health Sciences |
14.2.4.Celgene Corporation |
14.2.5.Alexion Pharmaceuticals Inc.. |
14.2.6.Bayer Healthcare AG |
14.2.7.CSL Behring |
14.2.8.Shire PLC |
14.2.9.Pfizer Inc. |
14.2.10.Celgene Corporation |
14.2.11.Amgen Inc. |
14.2.12.Novartis AG |
14.2.13.Bristol Myers Squibb |
14.2.14.Hoffmann-La Roche Ltd |
14.2.15.Emmaus Medical, Inc. |
15. Research Methodology |
16. Appendix and Abbreviations |
Key Market Players