Rare Hematology Disorders Market: By Disease Indication, By Treatment, By Patient, and By Geography

Rare Hematology Disorders Market Size, Share, Growth, Trends, and Global Industry Analysis: By Disease Indication (Rare Blood Cancers, Platelet-based Disorders, Plasma-based Disorders, and Others), By Treatment (Recombinant Factors, Plasma-derived Factors, Gene Therapies, and Other Therapies), By Patient ( Adults and Paediatrics), and By Region

Rare Hematology Disorders market size was valued at US$ 14.3 billion in 2023 and is poised to grow at a CAGR of 5.7% from 2024 to 2030. The market is poised for significant growth in the coming years, driven by increased awareness of rare blood disorders, coupled with advancements in diagnostic techniques like genetic testing, several governments have implemented policies and incentives to encourage research and development of treatments for rare diseases, including rare blood disorders. These initiatives provide financial and regulatory support, This, in turn, fuels the market for treatment options. Despite the promising growth potential, the rare hematology disorders market also faces some challenges like the high cost of treatment, fragmented market, and limited clinical trial data, due to the small patient population, conducting extensive clinical trials for rare blood disorders can be challenging.

Further, several key trends are shaping the future of the rare hematology disorders market focusing on personalized medicine, a rise of gene therapies which creates an opportunity for developing Orphan drug designation and exclusivity in emerging markets by collaboration between pharmaceutical companies, academic institutions, and patient advocacy groups can accelerate research and development efforts, leading to the creation of more effective and affordable treatments for rare blood disorders.

Rare Hematology Disorders Market Key Developments:
  • In February 2023, Amgen acquired Tenevra Bio for $900 million, gaining access to Tenevra's experimental gene therapy for beta-thalassemia, a rare blood disorder.
  • In December 2022, bluebird bio acquired Cellectis for $2 billion, aiming to combine their expertise in cell and gene therapies for various blood disorders, including sickle cell disease and beta-thalassemia.

Rare Hematology Disorders Market Summary

Study Period

2024 - 2030

Base Year

2023

CAGR

5.7%

Largest Market

Asia Pacific

Fastest Growing Market

Asia Pacific

Rare Hematology Disorders Market Dynamics

The market is experiencing significant growth driven by rising awareness and diagnosis, growing demand for specialized treatments, government support and orphan drug incentives, and technological advancements in gene editing, and gene therapy, which are leading to earlier and more accurate diagnoses, the demand for specialized and targeted therapies is rising. This creates opportunities for pharmaceutical companies to develop novel drugs and treatment modalities and other biotechnologies that offer promising avenues for developing curative treatments for rare blood disorders, and the market is witnessing a growing shift towards personalized medicine, tailoring treatments to individual patient's specific genetic makeup and disease characteristics. This approach holds promise for improving treatment efficacy and patient outcomes. These innovations hold immense potential to revolutionize the market landscape.

Rare Hematology Disorders Market Segmentation Analysis

Report Benchmarks

Details

Report Study Period

2024 - 2030

Market Size in 2023

US$ 14.3 billion

Market CAGR

5.7%

By Disease Indication

  • Rare blood cancers,
  • Platelet-based disorders
  • Plasma-based disorders
  • Others 

By Treatment

  • Recombinant factors
  • Plasma-derived factors
  • Gene therapies
  • Other therapies

By Patient

  • Adults
  • Paediatrics

Key Features of the Report

  • The report provides granular level information about the market size, regional market share, historic market (2019-2023), and forecast (2024-2030)
  • The report covers in-detail insights about the competitor’s overview, company share analysis, key market developments, and key strategies.
  • The report outlines drivers, restraints, unmet needs, and trends that are currently affecting the market.
  • The report tracks recent innovations, key developments, and start-up details that are actively working in the market.
  • The report provides a plethora of information about market entry strategies, regulatory framework, and reimbursement scenarios.

Download Free Sample Report

Frequently Asked Questions

Rare hematology disorders Market market size was valued at US$ 14.3 billion in 2023 and is expected to grow at a CAGR of 5.7% from 2024 to 2030.

Novo Nordisk A/S, Sanofi, PRA Health Sciences, Celgene Corporation, Alexion Pharmaceuticals, Inc.. Bayer Healthcare AG, CSL Behring, Shire PLC, Pfizer Inc., Celgene Corporation, Amgen Inc., Novartis AG, Bristol Myers Squibb, F. Hoffmann-La Roche Ltd, Emmaus Medical, Inc.

Asia-Pacific is the fastest growing and North America is the dominant market in rare hematology disorders market.

Author image

Author

Muni Kumar Meravath

Muni Kumar Meravath is a seasoned Healthcare Market Research Analyst with over 6 years of experience in the healthc.....

1.Executive Summary
2.Global Rare Hematology Disorders Market Introduction 
2.1.Global Rare Hematology Disorders Market  - Taxonomy
2.2.Global Rare Hematology Disorders Market  - Definitions
2.2.1.Disease Indication
2.2.2.Treatment
2.2.3.Patient
2.2.4.Region
3.Global Rare Hematology Disorders Market Dynamics
3.1. Drivers
3.2. Restraints
3.3. Opportunities/Unmet Needs of the Market
3.4. Trends
3.5. Product Landscape
3.6. New Product Launches
3.7. Impact of COVID 19 on Market
4.Global Rare Hematology Disorders Market Analysis, 2019 - 2023 and Forecast 2024 - 2030
4.1.  Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million)
4.2.  Year-Over-Year (Y-o-Y) Growth Analysis (%) 
4.3.  Market Opportunity Analysis 
5.Global Rare Hematology Disorders Market  By Disease Indication, 2019 - 2023 and Forecast 2024 - 2030 (Sales Value USD Million)
5.1. Rare blood cancers,
5.1.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million)
5.1.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) 
5.1.3. Market Opportunity Analysis 
5.2. Platelet-based disorders
5.2.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million)
5.2.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) 
5.2.3. Market Opportunity Analysis 
5.3. Plasma-based disorders
5.3.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million)
5.3.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) 
5.3.3. Market Opportunity Analysis 
5.4. Others 
5.4.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million)
5.4.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) 
5.4.3. Market Opportunity Analysis 
6.Global Rare Hematology Disorders Market  By Treatment, 2019 - 2023 and Forecast 2024 - 2030 (Sales Value USD Million)
6.1. Recombinant factors
6.1.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million)
6.1.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) 
6.1.3. Market Opportunity Analysis 
6.2. Plasma-derived factors
6.2.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million)
6.2.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) 
6.2.3. Market Opportunity Analysis 
6.3. Gene therapies
6.3.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million)
6.3.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) 
6.3.3. Market Opportunity Analysis 
6.4. Other therapies
6.4.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million)
6.4.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) 
6.4.3. Market Opportunity Analysis 
7.Global Rare Hematology Disorders Market  By Patient, 2019 - 2023 and Forecast 2024 - 2030 (Sales Value USD Million)
7.1. Adults
7.1.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million)
7.1.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) 
7.1.3. Market Opportunity Analysis 
7.2. Paediatrics
7.2.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million)
7.2.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) 
7.2.3. Market Opportunity Analysis 
8.Global Rare Hematology Disorders Market  By Region, 2019 - 2023 and Forecast 2024 - 2030 (Sales Value USD Million)
8.1. North America
8.1.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million)
8.1.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) 
8.1.3. Market Opportunity Analysis 
8.2. Europe
8.2.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million)
8.2.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) 
8.2.3. Market Opportunity Analysis 
8.3. Asia Pacific (APAC)
8.3.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million)
8.3.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) 
8.3.3. Market Opportunity Analysis 
8.4. Middle East and Africa (MEA)
8.4.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million)
8.4.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) 
8.4.3. Market Opportunity Analysis 
8.5. Latin America
8.5.1. Market Analysis, 2019 - 2023 and Forecast, 2024 - 2030, (Sales Value USD Million)
8.5.2. Year-Over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%) 
8.5.3. Market Opportunity Analysis 
9.North America Rare Hematology Disorders Market ,2019 - 2023 and Forecast 2024 - 2030 (Sales Value USD Million)
9.1. Disease Indication Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
9.1.1.Rare blood cancers,
9.1.2.Platelet-based disorders
9.1.3.Plasma-based disorders
9.1.4.Others 
9.2.  Treatment Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
9.2.1.Recombinant factors
9.2.2.Plasma-derived factors
9.2.3.Gene therapies
9.2.4.Other therapies
9.3.  Patient Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
9.3.1.Adults
9.3.2.Paediatrics
9.4.  Country Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
9.4.1.United States of America (USA)
9.4.2.Canada
10.Europe Rare Hematology Disorders Market ,2019 - 2023 and Forecast 2024 - 2030 (Sales Value USD Million)
10.1. Disease Indication Analysis  and Forecast  by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
10.1.1.Rare blood cancers,
10.1.2.Platelet-based disorders
10.1.3.Plasma-based disorders
10.1.4.Others 
10.2.  Treatment Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
10.2.1.Recombinant factors
10.2.2.Plasma-derived factors
10.2.3.Gene therapies
10.2.4.Other therapies
10.3.  Patient Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
10.3.1.Adults
10.3.2.Paediatrics
10.4.  Country Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
10.4.1.Germany
10.4.2.France
10.4.3.Italy
10.4.4.United Kingdom (UK)
10.4.5.Spain
11.Asia Pacific (APAC) Rare Hematology Disorders Market ,2019 - 2023 and Forecast 2024 - 2030 (Sales Value USD Million)
11.1. Disease Indication Analysis  and Forecast  by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
11.1.1.Rare blood cancers,
11.1.2.Platelet-based disorders
11.1.3.Plasma-based disorders
11.1.4.Others 
11.2.  Treatment Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
11.2.1.Recombinant factors
11.2.2.Plasma-derived factors
11.2.3.Gene therapies
11.2.4.Other therapies
11.3.  Patient Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
11.3.1.Adults
11.3.2.Paediatrics
11.4.  Country Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
11.4.1.China
11.4.2.India
11.4.3.Australia and New Zealand (ANZ)
11.4.4.Japan
11.4.5.Rest of APAC
12.Middle East and Africa (MEA) Rare Hematology Disorders Market ,2019 - 2023 and Forecast 2024 - 2030 (Sales Value USD Million)
12.1. Disease Indication Analysis  and Forecast  by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
12.1.1.Rare blood cancers,
12.1.2.Platelet-based disorders
12.1.3.Plasma-based disorders
12.1.4.Others 
12.2.  Treatment Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
12.2.1.Recombinant factors
12.2.2.Plasma-derived factors
12.2.3.Gene therapies
12.2.4.Other therapies
12.3.  Patient Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
12.3.1.Adults
12.3.2.Paediatrics
12.4.  Country Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
12.4.1.GCC Countries
12.4.2.South Africa
12.4.3.Rest of MEA
13.Latin America Rare Hematology Disorders Market ,2019 - 2023 and Forecast 2024 - 2030 (Sales Value USD Million)
13.1. Disease Indication Analysis  and Forecast  by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
13.1.1.Rare blood cancers,
13.1.2.Platelet-based disorders
13.1.3.Plasma-based disorders
13.1.4.Others 
13.2.  Treatment Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
13.2.1.Recombinant factors
13.2.2.Plasma-derived factors
13.2.3.Gene therapies
13.2.4.Other therapies
13.3.  Patient Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
13.3.1.Adults
13.3.2.Paediatrics
13.4.  Country Analysis 2019 - 2023 and Forecast 2024 - 2030 by Sales Value USD Million, Y-o-Y Growth (%), and Market Share (%) 
13.4.1.Brazil
13.4.2.Mexico
13.4.3.Rest of LA
14. Competition Landscape
14.1.  Market Player Profiles (Introduction, Brand/Product Sales, Financial Analysis, Product Offerings, Key Developments, Collaborations, M & A, Strategies, and SWOT Analysis) 
14.2.1.Sanofi
14.2.2.Novo Nordisk A/S
14.2.3.PRA Health Sciences
14.2.4.Celgene Corporation
14.2.5.Alexion Pharmaceuticals Inc..
14.2.6.Bayer Healthcare AG
14.2.7.CSL Behring
14.2.8.Shire PLC
14.2.9.Pfizer Inc.
14.2.10.Celgene Corporation
14.2.11.Amgen Inc.
14.2.12.Novartis AG
14.2.13.Bristol Myers Squibb
14.2.14.Hoffmann-La Roche Ltd
14.2.15.Emmaus Medical, Inc.
15. Research Methodology 
16. Appendix and Abbreviations 

Key Market Players

  • Sanofi
  • Novo Nordisk A/S
  • PRA Health Sciences
  • Celgene Corporation
  • Alexion Pharmaceuticals Inc..
  • Bayer Healthcare AG
  • CSL Behring
  • Shire PLC
  • Pfizer Inc.
  • Celgene Corporation
  • Amgen Inc.
  • Novartis AG
  • Bristol Myers Squibb
  • Hoffmann-La Roche Ltd
  • Emmaus Medical, Inc.

Related Industry Reports